Videos of channel "UC1YVq-XQ8FA3-ONbi7QScHg", see also playlists
#1 / 1:01:30 /
1.1K views /
1 month ago /
Webinar: Community Update with ITF Therapeutics: Introducing DUVYZAT™ (givinostat) [March 2024]
#2 / 45:03 /
349 views /
1 month ago /
Webinar: Sarepta Therapeutics - Data update from MOMENTUM study, SRP-5051 [Mar 2024]
#3 / 39:33 /
235 views /
1 month ago /
Webinar: NS Pharma - Overview of New Exon Skipping Trials: Brogidirsen and NS-050/NCNP-03 (Mar 2024)
#4 / 29:09 /
241 views /
1 month ago /
Webinar: PTC Therapeutics — EMFLAZA® Landscape in 2024
#5 / 52:15 /
279 views /
2 months ago /
Webinar: Overview of WVE-N531 and the FORWARD-53 Clinical Trial with Wave Life Sciences [Feb 2024]
#6 / 53:00 /
324 views /
2 months ago /
Webinar: Dyne Therapeutics — Advancing DYNE-251, an Investigational Medicine for DMD [Jan 2024]
#7 / 1:00:58 /
386 views /
3 months ago /
Navigating Steroid Choices: Understanding the Process, Pathways, and Policies
#8 / 13:27 /
298 views /
4 months ago /
Gene Therapy & Antibodies (Innovation Conversation with Barry Byrne, MD, PhD)
#9 / 1:03:41 /
475 views /
4 months ago /
Webinar: Community Update on the New INSPIRE DUCHENNE Clinical Study of SGT-003
#10 / 1:00:42 /
623 views /
5 months ago /
Webinar: AGAMREE® Approval with Catalyst Pharmaceuticals, Inc. [Nov 2023]
#11 / 59:55 /
1K views /
5 months ago /
Webinar: Overview of Topline Results from Phase 3 EMBARK Study
#12 / 50:51 /
1K views /
5 months ago /
AGAMREE Approval: What this means for you and your family
#13 / 25:01 /
115 views /
6 months ago /
Advocating for Access: Overview of Medicaid DUR and P&T Meetings
#14 / 54:28 /
1K views /
6 months ago /
Capricor Therapeutics: CAP-1002 HOPE-3 Program Update
#15 / 49:31 /
592 views /
6 months ago /
Edgewise Therapeutics: A Novel Approach Designed to Protect Muscle in Becker Muscular Dystrophy
#16 / 59:38 /
108 views /
6 months ago /
Supporting Families Through Decision Making
#17 / 52:31 /
442 views /
6 months ago /
Webinar: Affinity Duchenne™ and Affinity Beyond™: Updates on Investigational RGX-202 from REGENXBIO
#18 / 31:23 /
137 views /
7 months ago /
Advocating for Access: Insurance 101
#19 / 7:21 /
197 views /
7 months ago /
Research Row Presentation: Viltepso (NS Pharma) - PPMD 2023 Annual Conference
#20 / 29:12 /
308 views /
8 months ago /
Advocating for Access: Navigating Approved Therapies in Duchenne
#21 / 4:03 /
2.3K views /
9 months ago /
ELEVIDYS and Genetic Variants
#22 / 1:00:50 /
363 views /
9 months ago /
Research Row Breakout Session: PPMD Supported Research -- PPMD 2023 Annual Conference
#23 / 59:37 /
582 views /
9 months ago /
Research Row Breakout Session: Approved or on the Horizon -- PPMD 2023 Annual Conference
#24 / 16:26 /
76 views /
9 months ago /
Turning Adversity into Action: Your Power -- PPMD 2023 Annual Conference
#25 / 54:57 /
575 views /
9 months ago /
Gene Therapy: The Power of Advocacy & Real World Evidence -- PPMD 2023 Annual Conference
#26 / 11:49 /
138 views /
9 months ago /
Closing Remarks & Thank You -- PPMD 2023 Annual Conference
#27 / 29:14 /
38 views /
9 months ago /
Ethics and Fair Play -- PPMD 2023 Annual Conference
#28 / 52:15 /
221 views /
9 months ago /
Combination Therapies: How do We Get There? -- PPMD 2023 Annual Conference
#29 / 1:05:25 /
171 views /
9 months ago /
Battling Behaviors -- PPMD 2023 Annual Conference
#30 / 1:15:51 /
379 views /
9 months ago /
More than Puberty: The Impact of Testosterone -- PPMD 2023 Annual Conference